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Sharron – Renal Transplant
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ASGCT 2024
Presentation: A Highly Potent Engineered AAV Capsid, STAC-150, Enables High-Throughput AAV Production and Arrayed Epigenetic Regulator Screening Directly in Cultured Neurons
May 10th, 2024
Presentation: Directed Evolution of Bxb1 for the Development of Modular Integrases (MINTS)
May 9th, 2024
Presentation: Identification and Characterization of STAC-BBB, an Engineered AAV Capsid That Exhibits Widespread Transduction of the Central Nervous System in Cynomolgus Macaques
May 9th, 2024
Poster: Site-directed integration of large DNA sequences into endogenous sites in the human genome using engineered Modular Integrases (MINTS)
May 8th, 2024
Poster: Highly Specific Zinc Finger Proteins with Synthetic Target Sites Enable Self-Regulated Expression of Dosage-Sensitive Transgenes
May 8th, 2024
Poster: Zinc Finger Mediated Repression and Replacement of MFN2 Leads to the Rescue of Cellular Disease Phenotype in CMT2A Patient-Derived Cells
May 8th, 2024
Poster: Process and Formulation Development for a Novel Blood-Brain Barrier Penetrant AAV Capsid
May 8th, 2024
Poster: Unraveling Impact of Manufacturing Process-Related Stresses on AAV Stability, Aggregation, and DNA Release
May 8th, 2024
Poster: Development of Blood-Brain Barrier Penetrant AAVs through Receptor-Targeted Capsid Engineering
May 8th, 2024
Poster: Optimal Drug Product Presentation and Container Closure Selection for AAV-Based Genomic Medicines
May 8th, 2024