Accelerated Approval pathway for our ST-920 gene therapy product candidate for the treatment of Fabry disease.
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Expanded Access Policy
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Bryan – Fabry Disease
Lori – Fabry Disease
Matt – Fabry Disease
Elizabeth – Fabry Disease
Israel – Hemophilia A
Miles – Hemophilia A
Trevor – Prion Disease
Sharron – Renal Transplant
Patient Focus
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Overview
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Events
Presentations
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Miles’ Story
Hemophilia A
Hemophilia
Miles
June 12th, 2021
Israel
June 12th, 2021