Scientific & Medical Presentations

ASGCT 2021

Selective Repression of C9ORF72 Repeat Expansion-Containing Sense and Antisense Transcripts for the Treatment of ALS
ASGCT 2021

Zinc Finger Protein Transcription Factors Targeting Alpha-synuclein – A Promising Therapeutic Strategy for Parkinson’s Disease
AD/PD 2021

Zinc Finger Protein Transcription Factor-Mediated Repression of Alpha-Synuclein Expression as a Therapeutic Approach for Parkinson’s Disease
WORLDSymposium 2021

A Phase I/II Multicenter Gene Therapy Clinical Study for Fabry Disease