Hematology

In vivo genome editing restores haemostasis in a mouse model of haemophilia.
August 24th, 2018
State of the art: gene therapy of haemophilia.
August 24th, 2018
Functional footprinting of regulatory DNA.
August 24th, 2018
Long-Term Engraftment and Fetal Globin Induction upon BCL11A Gene Editing in Bone-Marrow-Derived CD34+ Hematopoietic Stem and Progenitor Cells.
August 24th, 2018
Genetic Targeting of the Albumin Locus to Treat Hemophilia.
August 24th, 2018
In vivo genome editing of the albumin locus as a platform for protein replacement therapy.
August 24th, 2018