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WORLD
Symposium
™ 2024
Clinical
WORLDSymposium 2024
Presentation: Updated results from ongoing phase 1/2 study (STAAR) for Isaralgagene civaparvovec (ST-920) gene therapy in adults with Fabry disease
WORLDSymposium 2024
Poster: Updated results from ongoing phase 1/2 study (STAAR) for Isaralgagene civaparvovec (ST-920) gene therapy in adults with Fabry disease
WORLDSymposium 2024
Poster: Anti-AAV6 antibody assay for patient enrollment supporting ST-920 phase 1/2 study for Fabry disease
Nonclinical
WORLDSymposium 2024
Presentation: A 3-month gene therapy single-dose IV administration pharmacology and safety study with isaralgagene civaparvovec (ST-920) for Fabry disease in mice
WORLDSymposium 2024
Poster: A 3-month gene therapy single-dose IV administration pharmacology and safety study with isaralgagene civaparvovec (ST-920) for Fabry disease in mice